In these babies we had to give the medication to prevent the blood from clotting, which had little effect on the behaviour.”
The discovery raises the possibility of treatment that could slow the progression of the disease.
The fact is that these results can be translated to patients, for example, by postponing or even reversing the early onset of symptoms.
“It may not be the best solution to prevent renal failure and therefore, we envisage that it will become vitally important to ascertain which patients have proton therapy, so that we can intervene sooner if symptoms develop due to proton therapy.
